Rare Disease Video - Niemann-Pick Disease Types A & B - National Organization for Rare Disorders
Por um escritor misterioso
Last updated 12 abril 2025
Niemann-Pick disease types A and B (NORD): Video

A blog about rare disease and films about rare diseases. — DISORDER: The Rare Disease Film Festival

Rare Diseases Research: Clinical Trial for Niemann-Pick Type C

Clinical disease characteristics of patients with Niemann-Pick Disease Type C: findings from the International Niemann-Pick Disease Registry (INPDR), Orphanet Journal of Rare Diseases

New Treatments May Be Available for Niemann-Pick Disease Soon

Niemann–Pick Disease Type C: Induced Pluripotent Stem Cell–Derived Neuronal Cells for Modeling Neural Disease and Evaluating Drug Efficacy - Daozhan Yu, Manju Swaroop, Mengqiao Wang, Ulrich Baxa, Rongze Yang, Yiping Yan, Turhan

Niemann Pick Disease - an overview

PDF) Niemann-Pick disease type C symptomatology: An expert-based clinical description

Rare diseases hi-res stock photography and images - Alamy

International Niemann-Pick Disease Registry (@inpdr_registry) / X
NPSuisse - Schweizerische Niemann Pick Vereinigung

Current & future challenges in clinical research of rare diseases
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